In honor of World Blindness Awareness Month, "GMA" is spotlighting a breakthrough gene therapy that's helping some blind ...
A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two ...
In a world first, a bespoke gene-editing therapy benefitted one child. Now reseachers plan to launch a clinical trial of the ...
A top US regulator plans to unveil a faster approach to approving custom gene-editing treatments, a move designed to unleash a wave of industry investment that will yield cures for patients with rare ...
In a first for adults in Singapore, scientists are conducting gene editing trials on heart patients to correct defects at ...
The U.S. Food and Drug Administration has placed a clinical hold on Intellia Therapeutics' two late-stage trials testing an ...
UniQure's therapy, called AMT-130, reduced disease progression by 75% at 36 months in patients who received a high dose.
Researchers announce breakthrough results for AMT-130, the first disease-modifying treatment for Huntington's disease, with ...
The FDA has officially placed two of Intellia’s Phase III studies under clinical hold after the biotech reported earlier this ...
ABC 11 Raleigh, NC on MSN
Duke Eye Center pioneers new gene therapy for rare eye disease
Duke Eye Center has become the first academic medical center in the country to implant a new cell-based gene therapy for a ...
Some of the most expensive drugs currently in use are gene therapies to treat specific diseases, and their high cost limits ...
Intellia earlier this year reported a similar grade 4 liver enzyme elevation associated with the gene therapy nexiguran ...
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