For children born with severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID), an investigational ...
Elania is one of 59 children born with ADA-SCID who have been cured using this gene therapy, which will soon be submitted for ...
Until recently, even the most advanced gene therapies could only be given after a child was born—often racing against time to prevent irreversible damage. In the first part of this series, we explored ...
LONDON -- A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on ...
Gene therapy has allowed several children born with inherited deafness to hear. A small study published Wednesday documents significantly restored hearing in five of six kids treated in China. On ...
Study flowchart and sample screening process. a Screening process for 1538 study participants. b Selection of groups with distinct control effects based on quartiles. CYL, cylinder; SE, spherical ...
CHICAGO -- Women are going for breast cancer gene testing in record numbers, forcing more parents to face a tough question: Should we test the kids? About 100,000 tests for breast cancer gene ...