In honor of World Blindness Awareness Month, "GMA" is spotlighting a breakthrough gene therapy that's helping some blind ...

The U.S. Food and Drug Administration has placed a clinical hold on Intellia Therapeutics' two late-stage trials testing an ...

In a first for adults in Singapore, scientists are conducting gene editing trials on heart patients to correct defects at ...

In 1962, a pediatric neurology resident at Columbia's Neurological Institute and his colleagues in the College of Physicians ...

Some of the most expensive drugs currently in use are gene therapies to treat specific diseases, and their high cost limits ...

An increasing demand for gene therapies is focusing the industry on enhancing production capabilities, transitioning from ...

The Boston biotech founded by Harvard professor David Sinclair is testing whether cellular reprogramming can turn back the ...

BioMarin no longer expects to hit its $4 billion revenue target by 2027, citing various market factors such as impending ...

FDA moves to speed biosimilar approvals by eliminating comparative studies, aiming to lower drug costs and increase ...

A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two ...

Duke Eye Center has become the first academic medical center in the country to implant a new cell-based gene therapy for a ...

To solve this critical challenge, he founded Nephrogen in 2022, a biotech startup that uses AI and advanced screening to ...