In a first for adults in Singapore, scientists are conducting gene editing trials on heart patients to correct defects at ...

In a world first, a bespoke gene-editing therapy benefitted one child. Now reseachers plan to launch a clinical trial of the ...

The U.S. government is divesting from mRNA vaccines, but will other uses of the technology be spared? In a time of ...

Liz Wood, who lives in Beacon, is the founder of The MYT1L Project ( myraregene.org ), a foundation that supports families whose children are affected by a rare genetic disorder.

Cathy Tie, who launched her first biotech in SF's IndieBio, now leads Manhattan Genomics in controversial push to edit human ...

In honor of World Blindness Awareness Month, "GMA" is spotlighting a breakthrough gene therapy that's helping some blind ...

Intellia Therapeutics, Inc. is rated Hold due to uncertainty from dosing pause in its MAGNITUDE program for ATTR. Learn more ...

The Boston biotech founded by Harvard professor David Sinclair is testing whether cellular reprogramming can turn back the ...

Specialty drugs, especially biologics, will constitute a significant portion of global drug spending by 2029, driven by cancer care costs. Autoimmune diseases and multiple sclerosis are key short-term ...

Seven years after the first gene-edited babies were revealed, biotech startup Manhattan Genomics is reviving the idea of ...

This mental health condition, sometimes called skin picking or excoriation disorder, involves picking the skin so much that ...

Tom Golisano donates a record $50 million to University of Maryland Medical System for children's hospital enhancements.