A GROUNDBREAKING treatment based on research by Spanish scientists has helped children born with incurable deafness hear for ...
In a first for adults in Singapore, scientists are conducting gene editing trials on heart patients to correct defects at ...
In a world first, a bespoke gene-editing therapy benefitted one child. Now reseachers plan to launch a clinical trial of the ...
In the first part of this interview, Romanski tells PharmTech Group that while the field of oral dosage forms has not grown ...
The U.S. government is divesting from mRNA vaccines, but will other uses of the technology be spared? In a time of ...
Cathy Tie, who launched her first biotech in SF's IndieBio, now leads Manhattan Genomics in controversial push to edit human ...
Health Secretary Robert F. Kennedy Jr. called the treatment 'a powerful glimpse into the future of personalized medicine' ...
The FDA plans to introduce a faster approval process for custom gene-editing therapies, allowing combined trials for patients with related rare ...
As of May 2025, RGX-202 displayed favourable safety, with no serious adverse events (SAEs) and adverse events of special ...
Nonfactor therapies may reduce costs associated with bleeding-related hospitalizations and use of bypassing agents. One study ...
The startup is developing genomic medicines for kidney diseases using advanced lipid nanoparticle (LNP) technology to deliver ...
Duke Eye Center has become the first academic medical center in the country to implant a new cell-based gene therapy for a ...