In honor of World Blindness Awareness Month, "GMA" is spotlighting a breakthrough gene therapy that's helping some blind ...

The U.S. government is divesting from mRNA vaccines, but will other uses of the technology be spared? In a time of ...

In a first for adults in Singapore, scientists are conducting gene editing trials on heart patients to correct defects at ...

Some of the most expensive drugs currently in use are gene therapies to treat specific diseases, and their high cost limits ...

The Boston biotech founded by Harvard professor David Sinclair is testing whether cellular reprogramming can turn back the ...

In 1962, a pediatric neurology resident at Columbia's Neurological Institute and his colleagues in the College of Physicians ...

Scientists at The University of Texas at Austin have developed a revolutionary gene-editing method using bacterial retrons ...

Oncologists' experience with CGT has increased, with more patients treated and earlier lines of therapy being utilized.

The trial was small — just 12 children were treated in one or both ears — but it offers important lessons for researchers ...

Up to 60% of congenital and early-onset hearing loss is caused by genetic mutations in an inherited gene, and gene therapy ...

FDA moves to speed biosimilar approvals by eliminating comparative studies, aiming to lower drug costs and increase ...

BioMarin no longer expects to hit its $4 billion revenue target by 2027, citing various market factors such as impending ...